Validation of a mutated PRE sequence allowing high and sustained transgene expression while abrogating WHV-X protein synthesis: application to the gene therapy of WAS
2009
Zanta-Boussif, M.A., Charrier, S., Brice-Ouzet, A., Martin, S., Opolon, P., Thrasher, A.J., Hope, T.J. and Galy, A.:
Gene Ther 16 (2009) 605–619.