Press releases

Media contact: Stéphanie Bardon – communication@genethon.fr – 01.69.47.12.78

Genethon announces First Patient dosed in Clinical Trial of Investigational Gene therapy GNT 0004 for Duchenne Muscular Dystrophy

(read more)

Genethon, 30 years of pioneering research and innovation in treating rare diseases

(read more)

Genethon and WhiteLab Genomics join forces to enhance gene therapy through artificial intelligence

(read more)

Genethon is delighted about the launch of a gene therapy clinical trial for late-onset Pompe disease

(read more)

Genethon gets the green light from the ANSM to start an innovative gene therapy trial for Duchenne muscular dystrophy

(read more)

Genethon welcomes the submission to EMA of Marketing Authorisation Application for LUMEVOQ® Gene Therapy to Treat Vision Loss due to Leber Hereditary Optic Neuropathy (LHON)

GenSight Biologics, a french biopharma company, just submitted to EMAMarketing Autorisation Application for LUMEVOQ® Gene Therapy to Treat Vision Loss due to Leber Hereditary Optic Neuropathy (LHON), a rare, mitochondrial genetic disease, caused by mutation in the ND4 mitochondrial gene.

(read more)

A Genethon team succeeds in inhibiting the immune response linked to AAV, opening up the possibility of treating more patients by gene therapy

(read more)

Genethon welcomes the conclusive results of a gene therapy trial in Chronic Septic Granulomatosis, a rare disease of the immune system

(read more)

Genethon strengthens its collaboration with Sarepta Therapeutics for the development of the gene therapy product GNT0004 in Duchenne muscular dystrophy

(read more)

A gene therapy based clinical trial for Fanconi anemia patients offers its first successful results

(read more)

First in vivo proof-of-concept in Steinert’s myotonic dystrophy, a neuromuscular disease

(read more)

Towards a clinical trial for gamma-sarcoglycanopathy, limb-girdle muscular dystrophy

(read more)

Clinical Proof-of-Concept Data for OTL-102 for the Treatment of X-CGD

(read more)

Genethon announces dosing of the first patient with Crigler–Najjar Syndrome

(read more)

Co-administration of AAV Vectors with SVP-Rapamycin Enables Vector Re-administration in Pre-clinical Gene Therapy Study Published in Nature Communications by Généthon and Selecta Biosciences

(read more)