News

An effective gene therapy approach for dysferlin deficiencies

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Thermo Fischer Scientific 2009 prize

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Gene therapy: Production of the first batch of HIV-derived vectors in Europe for use in a human clinical trial

Genethon, the laboratory created and funded by the AFM (French Association against Myopathies) using donations from Téléthon, today announced that it has produced, controlled and released a batch of lentiviral vectors derived from the human immunodeficiency (HIV) virus for a gene therapy trial in humans in a rare immune deficiency. The… (read more)

Neuromuscular diseases: A pharmacological therapeutic approach for certain sarcoglycanopathies

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